About the Study

Severe combined immunodeficiency (SCID): A study to see how different amounts of a drug called busulfan help improve the immune system of infants after a stem cell transplant

This study is being done for infants: •Diagnosed with severe combined immunodeficiency (SCID). Researchers want to find out if lower doses of a chemotherapy drug called busulfan before stem cell transplant can help patients with Severe Combined Immune Deficiency (SCID).

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Full Study Name: A randomized trial of low versus moderate exposure busulfan for infants with severe combined immunodeficiency (SCID) receiving TCRαβ+/CD19+ depleted transplantation: A Phase II study by the Primary Immune Deficiency Treatment Consortium (PIDTC) and Pediatric Transplantation & Cellular Therapy Consortium (PTCTC)